Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
Biotech
Cell & Gene Therapy
Clinical Data
Venture Capital
Deals
Research
Medtech
Devices
Diagnostics
AI and Machine Learning
CRO
Special Reports
Trending Topics
Clinical Development
Biologics
Fierce 50
Special Report
Awards Gala
Resources
Fierce Events
Industry Events
Webinars
Podcasts
Whitepapers
Survey
Events
Subscribe
Trending T
Biotech
Cell & Gene Therapy
Clinical Data
Venture Capital
Deals
Research
Medtech
Devices
Diagnostics
AI and Machine Learning
CRO
Special Reports
Trending Topics
Clinical Development
Biologics
Fierce 50
Special Report
Awards Gala
Resources
Fierce Events
Industry Events
Webinars
Podcasts
Whitepapers
Survey
Events
Subscribe
Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
spinal muscular atrophy
Biotech
Phase 3 Scholar Rock trial hits SMA goal, sending stock up 327%
Investors went wild despite the higher dose falling short of the targeted efficacy and Scholar Rock making no mention of a key secondary goal.
Nick Paul Taylor
Oct 7, 2024 8:45am
Roche, Abu Dhabi partner to study rare spinal disease
May 23, 2024 5:30am
Novartis, Voyager launch $100M gene therapy mission
Jan 2, 2024 8:31am
David Liu's lab finds base editing may spur one-time SMA therapy
Mar 31, 2023 2:46pm
Celgene, Acceleron alum Backstrom tapped to lead Scholar Rock
Sep 20, 2022 11:20am
Scholar Rock bags $205M as 24-month data point to SMA durability
Jun 17, 2022 10:34am